Community, connection, collaboration

At Agios, building bonds and cultivating relationships are at the heart of our ability to create life-changing therapies for people with genetically defined diseases.

Patients and caregivers, advocates, healthcare providers, payers, scientific collaborators and research partners. We’re all part of a team that helps bring life-changing therapies to market for people with genetically defined diseases.

We’re committed to building trusted relationships with our extended teammates, each of whom lends mission-critical insight that enables us to discover, develop and deliver therapies faster and with greater success. We simply couldn’t do it without the unique contributions and perspectives of each person.

For patients,
and caregivers

At Agios, people living with genetically defined diseases are at the center of everything we do and every decision we make. Their needs, concerns, input and collaboration are essential to fulfilling our mission: to make a meaningful difference in patients’ lives and fundamentally change the way genetically defined diseases are treated.

If you or a loved one are living with a genetically defined disease, explore more about the ways we can partner together.

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PK deficiency patient support program

We offer a customized, comprehensive support program to help patients and caregivers learn more and navigate the challenges of living with the disease and provide support for accessing medicine. Sign up at and get connected with a dedicated Patient Support Manager.

Visit MyAgios

Resources for education and connection

We know that reliable information can be hard to come by. We can help. Check out our list of vetted Agios and third-party resources for patients and caregivers.

Explore Resources

Ongoing clinical studies

Our clinical programs explore investigational, oral treatment approaches for genetically defined diseases. Find out more about our programs and talk to your doctor if you’re interested in participating in studies that are currently recruiting.

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Resources for

We recognize and appreciate the significant role that physicians play in the lives of people with genetically defined diseases. They are a cornerstone of the community that treats and supports patients.

With medical information, grant opportunities, educational resources and treatment options, we aim to further their efforts on behalf of patients.

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for partnership

Great science requires great teamwork. By truly listening to and trusting partners, collaborators, healthcare providers, advocates, and patients we are able to identify and pursue the ideas that can make the biggest impact for people living with genetically defined diseases.

Explore our partnership opportunities and learn more about the ways we can work together to make a difference in patients’ lives.

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