Pyruvate kinase deficiency

Phase 3 Study (ACTIVATE) to Evaluate Efficacy and Safety of AG-348 in Not Regularly Transfused Adult Participants With Pyruvate Kinase Deficiency (PKD)

Pyruvate kinase deficiency

Phase 3 Study (ACTIVATE-T) Evaluating the Efficacy and Safety of AG-348 in Regularly Transfused Adult Participants With Pyruvate Kinase Deficiency (PKD)

Pyruvate kinase deficiency

Phase 2 DRIVE PK Study of AG-348 in Adult Patients With Pyruvate Kinase Deficiency

Pyruvate kinase deficiency

Pyruvate Kinase Deficiency Global Longitudinal Registry (PEAK Registry)

Thalassemia

A Phase 2, Open-label, Multicenter Study to Determine the Efficacy, Safety, Pharmacokinetics, and Pharmacodynamics of AG-348 in Adult Subjects With Non-transfusion-dependent Thalassemia